Gene Therapy for Rare Diseases

Gene Therapy mainly involves in the alteration of genetic material within a cell or organism with an intention of curing of the diseases. Both gene therapy and cell therapy are overlapping fields of biomedical research with the goals of repairing the direct cause of Genetic diseases in DNA or cellular population respectively, the discovery of recombinant DNA technology in the 1970s provided proof to develop gene therapy efficiently. Scientists use these techniques to readily manipulate viral genomes, isolate genes and identify mutations involved in human diseases, characterize and regulate gene expressions, and engineer various non- viral and viral vectors. Various long-term treatments for anemia, hemophilia, cystic fibrosis, muscular dystrophy, Gauscher’s disease, lysosomal storage diseases, cardiovascular diseases, diabetes and diseases of bones and joints are resolved through successful gene therapy.

 

  • Gene therapy for malignant melanoma
  • Gene therapy for sickle-cell disease
  • Development of regenerative treatment models
  • Different vectors for gene therapy
  • Gene therapy product

Related Conference of Gene Therapy for Rare Diseases

May 10-11, 2021

4th Global Experts Meeting on Infectious Diseases

Singapore City, Singapore
May 27-28, 2021

7th Rare Diseases and Orphan Drugs

Vienna, Austria
July 19-20, 2021

13th Global Infections Conference

Tokyo, Japan
September 06-07, 2021

11th World Congress on Rare Diseases and Orphan Drugs

Berlin, Germany
October 21-22, 2021

International Conference on Tropical Diseases and Cure

Zurich, Switzerland
November 22-23, 2021

3rd World Congress on Advancements in Tuberculosis and Lung Diseases

Singapore City, Singapore
February 07-08, 2022

9th International Congress on Infectious Diseases

Aberdeen, UK

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