Therapies for Rare Diseases
Critical insights in the advancement of gene and cell therapeutic disorders have opened up the likelihood of durably treating and potentially curing a number of uncommon rare genetic diseases. The present therapeutic methodologies include gene and cell therapy: In gene therapy, a conveyance vehicle (as an engineered virus) will convey a right form of the gene of interest or will mute the diseased gene in a patient’s cells. In cell therapy, an engineered cell line is utilized to present appropriately genetic conditions in order to reflect the intended therapeutic impact. There are targeted therapies developed to treat cancer at the malignant cellular level by affecting the biologic pathways particular to cancerous cells. It was the consequence of many years of research seeking to implement the biological mechanisms of the disease.
- Gene Therapy
- Immunotherapy
- Enzyme Replacement Therapy
- Renal replacement therapy
- Corticosteroid therapy
- Targeted RNAi Therapy Approach
Related Conference of Therapies for Rare Diseases
May 21-22, 2025
6th Annual Meeting on Infectious Diseases, Microbiology & Beneficial Microbes
Paris, France
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12th International Conference on Infectious Diseases, Bacteriology and Antibiotics
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September 22-23, 2025
11th International Conference on Infectious and Rare Diseases
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October 06-07, 2025
13th World Congress on Control and Prevention of HIV/AIDS, STDs & STIs
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20th World Conference on Infectious Diseases, Prevention and Control
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Therapies for Rare Diseases Conference Speakers
Recommended Sessions
- Rare Disease in Oncology
- Clinical Case Reports on Rare Diseases
- Clinical Research on Orphan Drugs
- Current research on Rare Diseases
- Genetic Diseases and Disorders
- Hematological Diseases
- Legal Issues Related to Rare Diseases
- Neurological Diseases
- Nursing and Rare Disease
- Other Rare Diseases
- Pediatric Rare Diseases
- Potency of Orphan Drugs
- Rare Aging Diseases
- Rare Diseases and its Cause
- Rare Diseases due to Plastic Surgery
- Rare diseases in Nephrology
- Rare diseases of Endocrine System
- Rare diseases of Genitourinary System
- Rare Diseases of Immune System
- Rare Diseases of Lymphatic System
- Rare Diseases of Sexual Health
- Rare Gynecological and Obstetrical Diseases
- Rare Hereditary Diseases
- Rare Metabolic Diseases
- Rare Ophthalmological Diseases
- Rare Oral Diseases
- Rare Pulmonary Diseases
- Rare Skin Diseases
- Strategies for Diagnosis &Treatment
- Therapies for Rare Diseases
- Undiagnosed Rare Diseases
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