Potency of Orphan Drugs

Orphan drugs are considered to be medicinal products intended for the diagnosis, prevention or the treatment of rare diseases. Approval of all drugs in rare diseases conditions must be based on effectivenessof substantial evidence of effectiveness in treating or preventing the condition with the evidence of safety for the treatment use. Over the last decade of 30 years, more than 400 medicines representing 447 separate medicinal indications have been approved to treat conditions and diseases symptoms rare diseases, compared to lesser than 10 in the 1970s

  • Nonclinical studies
  • Disease Pathophysiology
  • Chemistry, Manufacturing and Control

Related Conference of Potency of Orphan Drugs

June 02-03, 2025

14th World Congress on Rare Diseases and Orphan Drugs

Amsterdam, Netherlands
June 02-03, 2025

17th Euro-Global Conference on Infectious Diseases

Amsterdam, Netherlands
August 28-29, 2025

8th Pathology and Infectious Disease Conference

London, UK
September 22-23, 2025

11th International Conference on Infectious and Rare Diseases

Vancouver, Canada
December 11-12, 2025

8th Annual Congress on Bacterial, Viral and Infectious Diseases

Prague, Czech Republic

Potency of Orphan Drugs Conference Speakers

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