Therapies for Rare Diseases

Critical insights in the advancement of gene and cell therapeutic disorders have opened up the likelihood of durably treating and potentially curing a number of uncommon rare genetic diseases. The present therapeutic methodologies include gene and cell therapy: In gene therapy, a conveyance vehicle (as an engineered virus) will convey a right form of the gene of interest or will mute the diseased gene in a patient’s cells. In cell therapy, an engineered cell line is utilized to present appropriately genetic conditions in order to reflect the intended therapeutic impact. There are targeted therapies developed to treat cancer at the malignant cellular level by affecting the biologic pathways particular to cancerous cells. It was the consequence of many years of research seeking to implement the biological mechanisms of the disease.

  • Gene Therapy
  • Immunotherapy
  • Enzyme Replacement Therapy
  • Renal replacement therapy
  • Corticosteroid therapy
  • Targeted RNAi Therapy Approach

Related Conference of Therapies for Rare Diseases

May 11-12, 2017

4th International congress on Infectious Diseases

Barcelona, Spain
August 21-23, 2017

3rd Annual Congress on Infectious Diseases

San Francisco, California, USA
September 04-05, 2017

Global Experts Meeting on Sexually Transmitted Diseases

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September 7-9, 2017

6thEuro-Global Conference on Infectious Diseases

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September 13-14, 2017

6th Annual Bacteriology and Parasitology Meeting

October 30-November 1, 2017

3rd Annual Congress on Rare Diseases and Orphan Drugs

(10 Plenary Forums - 1 Event)
San Antonio, Texas, USA

Therapies for Rare Diseases Conference Speakers

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