Challenges in Rare Diseases Treatment

There are approximately 7,000 rare diseases, which from a regulatory perspective are defined as those diseases where there are less than 200,000 patients in the US or that affect no more than five in 10,000 of the general population in the EU. "Orphan drugs" are medicinal products intended for diagnosis, prevention or treatment of life-threatening or debilitating rare diseases. They are "orphans" because the pharmaceutical industry has little interest under normal market conditions in developing and marketing drugs intended for only a small number of patients suffering from very rare conditions.

  • Different types of rare diseases
  • Misperceptions about rare diseases
  • Role of Patient Registries
  • Regulatory Approaches and Alternative Methodologies
  • Rising Patient Costs
  • Reimbursement Strategies

Related Conference of Challenges in Rare Diseases Treatment

August 21-23, 2017

3rd Annual Congress on Infectious Diseases

San Francisco, California, USA
September 7-9, 2017

6thEuro-Global Conference on Infectious Diseases

Paris, France
September 13-14, 2017

6th Annual Bacteriology and Parasitology Meeting

Singapore
October 30-November 1, 2017

3rd Annual Congress on Rare Diseases and Orphan Drugs


(10 Plenary Forums - 1 Event)
San Antonio, Texas, USA
November 06-07, 2017

3rd International Conference on Flu and Emerging Infectious Diseases

Las Vegas, Nevada, USA
March 1-2, 2018

5th International congress on Infectious Diseases

Berlin, Germany
June 11-12, 2018

4th World Congress on Rare Diseases and Orphan Drugs

Dublin, Ireland
31st August-1st September 2018

International Conference on Emerging Infectious Diseases

Zurich, Switzerland

Challenges in Rare Diseases Treatment Conference Speakers

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